What are the Treatment Options for Wiskott-Aldrich Syndrome?
Management of WAS is multidisciplinary and may include:
Hematopoietic Stem Cell Transplantation (HSCT): The only curative treatment, which involves replacing the defective immune system with a healthy one from a compatible donor. Symptomatic Treatment: Management of eczema with topical treatments, and use of immunoglobulin replacement therapy to reduce infections. Platelet Transfusions: To manage severe thrombocytopenia. Antibiotics and Antivirals: Prophylactic and therapeutic use to prevent and treat infections. Gene Therapy: An emerging treatment option that involves correcting the defective gene in the patient's own stem cells.
