crispr based epigenome editing

What Conditions Could Benefit from This Technology?

Several pediatric conditions could potentially benefit from CRISPR based epigenome editing, including:
- Genetic Disorders: Diseases like Duchenne muscular dystrophy, spinal muscular atrophy, and Rett syndrome.
- Neurodevelopmental Disorders: Conditions such as autism spectrum disorders and intellectual disabilities.
- Metabolic Disorders: Diseases like phenylketonuria and glycogen storage diseases.
- Cancers: Pediatric cancers such as neuroblastoma and leukemia.

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