What Conditions Could Benefit from This Technology?
Several pediatric conditions could potentially benefit from CRISPR based epigenome editing, including: - Genetic Disorders: Diseases like Duchenne muscular dystrophy, spinal muscular atrophy, and Rett syndrome. - Neurodevelopmental Disorders: Conditions such as autism spectrum disorders and intellectual disabilities. - Metabolic Disorders: Diseases like phenylketonuria and glycogen storage diseases. - Cancers: Pediatric cancers such as neuroblastoma and leukemia.