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spinal muscular atrophy (sma)
What are the Treatment Options for SMA?
While there is no cure for SMA, recent advances have led to the development of treatments that can improve outcomes. Key treatments include:
Nusinersen (Spinraza)
: An antisense oligonucleotide therapy that increases the production of the SMN protein.
Onasemnogene abeparvovec-xioi (Zolgensma)
: A gene therapy that delivers a functional copy of the SMN1 gene.
Risdiplam (Evrysdi)
: An oral medication that increases SMN protein levels.
Supportive care is also crucial and includes respiratory support, nutritional support, physical therapy, and orthopedic interventions.
Frequently asked queries:
What is Spinal Muscular Atrophy (SMA)?
What Causes SMA?
What are the Types of SMA?
How is SMA Diagnosed?
What are the Treatment Options for SMA?
What is the Prognosis for Children with SMA?
What Research is Being Conducted on SMA?
What are the Key Qualities of a Good Mentor in Pediatrics?
What Are the Advantages of RIC Hearing Aids for Children?
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What Are Insecticide Treated Bed Nets (ITNs)?
How Does Telemedicine Help in Overcoming Access Issues?
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How Are Robotics Being Utilized in Pediatric Surgery?
How Does it Manifest in Neonates?
What Does High IgM Indicate in Newborns?
How Can ECC Be Prevented?
How Do You Educate Children About Fire Safety?
What Are the Long-term Prognoses?
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