Smn Protein Replacement - Neonatal Disorders

Relevant Publications

Scoliosis Development in Spinal Muscular Atrophy: The Influences of Genetic Severity, Functional Level, and Disease-Modifying Treatments.

Issue Release: 2024

Advances in Disease-Modifying Therapeutics for Chronic Neuromuscular Disorders.

Issue Release: 2024

Recent Progress in Gene-Targeting Therapies for Spinal Muscular Atrophy: Promises and Challenges.

Issue Release: 2024

Emerging Gene Therapy Approaches in the Management of Spinal Muscular Atrophy (SMA): An Overview of Clinical Trials and Patent Landscape.

Issue Release: 2023

Gene Therapy for Spinal Muscular Atrophy (SMA): A Review of Current Challenges and Safety Considerations for Onasemnogene Abeparvovec (Zolgensma).

Issue Release: 2023

Gene therapy in spinal muscular atrophy.

Issue Release: 2023

Base editing as a genetic treatment for spinal muscular atrophy.

Issue Release: 2023

Boosting neuregulin 1 type-III expression hastens SMA motor axon maturation.

Issue Release: 2023

An Overview of the Therapeutic Strategies for the Treatment of Spinal Muscular Atrophy.

Issue Release: 2023

SMN regulates GEMIN5 expression and acts as a modifier of GEMIN5-mediated neurodegeneration.

Issue Release: 2023

Restoring SMN Expression: An Overview of the Therapeutic Developments for the Treatment of Spinal Muscular Atrophy.

Issue Release: 2022

New treatments in spinal muscular atrophy.

Issue Release: 2022

[Pharmacological and clinical profile of Onasemnogene Aveparvovec, the first gene therapy for spinal muscular atrophy (SMA)].

Issue Release: 2022

Progress in spinal muscular atrophy research.

Issue Release: 2022

Internal Introns Promote Backsplicing to Generate Circular RNAs from Spinal Muscular Atrophy Gene.

Issue Release: 2022

Onasemnogene abeparvovec for the treatment of spinal muscular atrophy.

Issue Release: 2022

Restoring Protein Expression in Neuromuscular Conditions: A Review Assessing the Current State of Exon Skipping/Inclusion and Gene Therapies for Duchenne Muscular Dystrophy and Spinal Muscular Atrophy.

Issue Release: 2021

Selecting disease-modifying medications in 5q spinal muscular atrophy.

Issue Release: 2021

Spinal Muscular Atrophy: The Use of Functional Motor Scales in the Era of Disease-Modifying Treatment.

Issue Release: 2021

Targeting the 5\' untranslated region of as a therapeutic strategy for spinal muscular atrophy.

Issue Release: 2021

Why are NRTIs Important in Pediatric Care?

What is Social Communication?

How Does Growth Affect Pediatric Anatomy?

What Are the Benefits of Group Counseling?

What are the Indications for a Sputum Culture in Pediatrics?

How is the Need for Special Education Determined?

What Techniques Does a CBT Therapist Use?

Are there Exceptions to Expiry Dates?

How Do Decision Support Tools Enhance Pediatric Care?

What Are the Components of Prenatal Care?

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